Buscar resultados de ensayos clínicos
Adenosine Deaminase Deficiency - 18 Studies Found
Estado | Estudiar |
Completed |
Nombre del estudio: Gene Therapy ADA Deficiency Condición: Adenosine Deaminase Deficiency Fecha: 2011-01-18 Intervenciones: Biological: Intravenous infusion of transduced cells Intravenous infusion of transduced cells |
Completed |
Nombre del estudio: Treatment of SCID Due to ADA Deficiency With Autologous Transplantation of Cord Blood or Hematopoietic CD 34+ Cells After Addition of a Normal Human ADA cDNA by the EFS-ADA Lentiviral Vector Condición:
|
Withdrawn |
Nombre del estudio: Quality of Life and Neuropsychiatric Sequelae in Patients Treated With Gene Therapy for ADA-SCID and in Their Parents Condición: ADA-SCID Fecha: 2010-08-14 |
Recruiting |
Nombre del estudio: Autologous Cryopreserved CD34+ Hematopoietic Cells Transduced With EFS-ADA Lentivirus for ADA SCID Condición: Severe Combined Immunodeficiency Due to ADA Deficiency Fecha: 2016-12-19 Intervenciones: Biological: Infusion of autologous cryopreserved EFS-ADA LV CD34+ cells Infusion of OTL-101 after reduce |
Recruiting |
Nombre del estudio: EZN-2279 in Patients With ADA-SCID Condición:
|
Recruiting |
Nombre del estudio: Lentiviral Gene Therapy for Adenosine Deaminase (ADA) Deficiency Condición:
|
Active, not recruiting |
Nombre del estudio: Autologous Transplant of EFS-ADA Modified Bone Marrow Cells for ADA-Deficient Severe Combined Immunodeficiency (SCID) Condición: ADA-SCID Fecha: 2013-05-07 Intervenciones: Genetic: EFS-ADA transduced CD34+ cells from the bone marrow Eligible subjects will undergo bone marrow |
Completed |
Nombre del estudio: Gene Therapy for ADA-SCID Condición: Severe Combined Immunodeficiency Syndrome Fecha: 2008-01-08 Intervenciones: Genetic: gene transduced PBL and/or gene transduced HSC infusions of autologous PBL and/or HSC transduce |
Active, not recruiting |
Nombre del estudio: ADA Gene Transfer Into Hematopoietic Stem/Progenitor Cells for the Treatment of ADA-SCID Condición: Immunologic Deficiency Syndromes Fecha: 2008-01-10 Intervenciones: Genetic: Gene transduced CD34+ cells infusion of autologous CD34+ cells transduced with retroviral vecto |
Recruiting |
Nombre del estudio: Participation in a Research Registry for Immune Disorders Condición:
|